Antisense therapy in neurology.
Ontology highlight
ABSTRACT:
SUBMITTER: Lee JJ
PROVIDER: S-EPMC4251390 | biostudies-literature | 2013 Aug
REPOSITORIES: biostudies-literature
Publications
Antisense therapy in neurology.
Lee Joshua J A JJ Yokota Toshifumi T
Journal of personalized medicine 20130802 3
Antisense therapy is an approach to fighting diseases using short DNA-like molecules called antisense oligonucleotides. Recently, antisense therapy has emerged as an exciting and promising strategy for the treatment of various neurodegenerative and neuromuscular disorders. Previous and ongoing pre-clinical and clinical trials have provided encouraging early results. Spinal muscular atrophy (SMA), Huntington's disease (HD), amyotrophic lateral sclerosis (ALS), Duchenne muscular dystrophy (DMD), F ...[more]
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