Systemic AAV Gene Therapy Close to Clinical Trials for Several Neuromuscular Diseases.
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ABSTRACT:
SUBMITTER: Wells DJ
PROVIDER: S-EPMC5383641 | biostudies-literature | 2017 Apr
REPOSITORIES: biostudies-literature
Publications
Systemic AAV Gene Therapy Close to Clinical Trials for Several Neuromuscular Diseases.
Molecular therapy : the journal of the American Society of Gene Therapy 20170322 4
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