Ontology highlight
ABSTRACT:
SUBMITTER: Qu Y
PROVIDER: S-EPMC6404499 | biostudies-literature | 2019 Jun
REPOSITORIES: biostudies-literature
Qu Yuan Y Liu Yi Y Noor Ahmed Fayyaz AF Tran Johnathan J Li Rui R
Neural regeneration research 20190601 6
Common neurodegenerative diseases of the central nervous system are characterized by progressive damage to the function of neurons, even leading to the permanent loss of function. Gene therapy via gene replacement or gene correction provides the potential for transformative therapies to delay or possibly stop further progression of the neurodegenerative disease in affected patients. Adeno-associated virus has been the vector of choice in recent clinical trials of therapies for neurodegenerative ...[more]