Ontology highlight
ABSTRACT:
SUBMITTER: Kyosen SO
PROVIDER: S-EPMC6868559 | biostudies-literature | 2019
REPOSITORIES: biostudies-literature
Kyosen Sandra Obikawa SO Toma Leny L Nader Helena Bonciani HB Nader Helena Bonciani HB Braga Marion Coting MC Pereira Vanessa Gonçalves VG Canossa Sueli S Pesquero João Bosco JB D'Almeida Vânia V Martins Ana Maria AM
Revista paulista de pediatria : orgao oficial da Sociedade de Pediatria de Sao Paulo 20190509 3
<h4>Objective</h4>To report the stabilization of urinary glycosaminoglicans (GAG) excretion and clinical improvements in patients with mucopolysaccharidosis type I (MPS I) under an alternative dose regimen of laronidase of 1.2 mg/kg every other week.<h4>Methods</h4>We participated in a dose-optimization trial for laronidase in MPS-I patients using four alternative regimens: 0.58 mg/kg every week, 1.2 mg/kg every two weeks, 1.2 mg/kg every week and 1.8 mg/kg every other week (EOW). After the tria ...[more]