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Promising AAV.U7snRNAs vectors targeting DMPK improve DM1 hallmarks in patient-derived cell lines

ABSTRACT: To evaluate the effect of AAV.U7snRNAs in the gene expression and alternative expression profiles of myotonic dystrophy cell lines.

ORGANISM(S): Homo sapiens

PROVIDER: GSE233947 | GEO | 2023/06/08

REPOSITORIES: GEO

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