Fragile X syndrome: an update on developing treatment modalities.
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ABSTRACT:
SUBMITTER: Healy A
PROVIDER: S-EPMC3369755 | biostudies-literature | 2011 Aug
REPOSITORIES: biostudies-literature
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Fragile X syndrome: an update on developing treatment modalities.
Healy Aileen A Rush Roger R Ocain Timothy T
ACS chemical neuroscience 20110322 8
Intellectual disability (ID; mental retardation) is considered an immutable condition. Current medical practices are aimed at relieving symptoms and not at altering the underlying cognitive deficits. Scientific advancements from the past decade have led to the exciting possibility that ID may now be treatable. Moreover, pharmaceutical therapies targeting the most common form of inherited ID, Fragile X syndrome (FXS), may become the new benchmark for central nervous system (CNS) drug discovery: s ...[more]
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