A new inducible transgenic mouse model for C9orf72-associated GGGGCC repeat expansion supports a gain-of-function mechanism in C9orf72-associated ALS and FTD.
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ABSTRACT:
SUBMITTER: Hukema RK
PROVIDER: S-EPMC4271461 | biostudies-literature | 2014 Dec
REPOSITORIES: biostudies-literature
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A new inducible transgenic mouse model for C9orf72-associated GGGGCC repeat expansion supports a gain-of-function mechanism in C9orf72-associated ALS and FTD.
Hukema Renate K RK Riemslagh Fréderike W FW Melhem Shamiram S van der Linde Herma C HC Severijnen Lies-Anne Wfm LA Edbauer Dieter D Maas Alex A Charlet-Berguerand Nicolas N Willemsen Rob R van Swieten John C JC
Acta neuropathologica communications 20141213
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