Ontology highlight
ABSTRACT:
SUBMITTER: Mercuri E
PROVIDER: S-EPMC4975396 | biostudies-literature | 2016
REPOSITORIES: biostudies-literature
Mercuri Eugenio E Coratti Giorgia G Messina Sonia S Ricotti Valeria V Baranello Giovanni G D'Amico Adele A Pera Maria Carmela MC Albamonte Emilio E Sivo Serena S Mazzone Elena Stacy ES Arnoldi Maria Teresa MT Fanelli Lavinia L De Sanctis Roberto R Romeo Domenico M DM Vita Gian Luca GL Battini Roberta R Bertini Enrico E Muntoni Francesco F Pane Marika M
PloS one 20160805 8
The advent of therapeutic approaches for Duchenne muscular dystrophy (DMD) has highlighted the need to identify reliable outcome measures for young boys with DMD. The aim of this study was to develop a revised version of the North Star Ambulatory Assessment (NSAA) suitable for boys between the age of 3 and 5 years by identifying age appropriate items and revising the scoring system accordingly. Using the scale in 171 controls between the age of 2.9 and 4.8 years, we identified items that were ap ...[more]