Ontology highlight
ABSTRACT:
SUBMITTER: George LA
PROVIDER: S-EPMC6142599 | biostudies-literature | 2017 Dec
REPOSITORIES: biostudies-literature
Hematology. American Society of Hematology. Education Program 20171201 1
Concurrent with the development of recombinant factor replacement products, the characterization of the <i>F9</i> and <i>F8</i> genes over 3 decades ago allowed for the development of recombinant factor products and made the hemophilias a target disease for gene transfer. The progress of hemophilia gene therapy has been announced in 3 American Society of Hematology scientific plenary sessions, including the first "cure" in a large animal model of hemophilia B in 1998, first in human sustained ve ...[more]