Ontology highlight
ABSTRACT:
SUBMITTER: Hagerman KA
PROVIDER: S-EPMC6590656 | biostudies-literature | 2019 Apr
REPOSITORIES: biostudies-literature
Hagerman Katharine A KA Howe Sarah J SJ Heatwole Chad R CR
Muscle & nerve 20190205 4
<h4>Introduction</h4>Myotonic dystrophy (DM) is a chronic, multisystemic, neurological condition. Patients and caregivers are uniquely suited to identify what symptoms are most important and highlight the unmet needs that are most relevant to DM.<h4>Methods</h4>We conducted a North American, cross-sectional study of people with DM type-1, congenital DM, and DM type-2 and their family members. We sent patients and caregivers separate surveys to identify and quantitate the issues of greatest impor ...[more]