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Therapeutic homology-independent targeted integration in retina and liver

ABSTRACT: We report the integration of AAV using CRISPr techonology within Mus musculus targeting RHO and ALB genes.

ORGANISM(S): Mus musculus

PROVIDER: GSE158759 | GEO | 2022/01/13

REPOSITORIES: GEO

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Therapeutic homology-independent targeted integration in retina and liver.

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