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Molecular and functional characterization of FD-iPSC derived neural crest precursor cells

ABSTRACT: Global gene expression analysis of FD-iPSC and deribved neural crest cells Here we report the derivation of patient specific Familial Dysautonomia-iPSCs and their directed differentiation into multiple cell types capable of modeling the tissue specific splicing defect in vitro.

ORGANISM(S): Homo sapiens

PROVIDER: GSE17043 | GEO | 2009/08/31

SECONDARY ACCESSION(S): PRJNA117847

REPOSITORIES: GEO

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Molecular and functional characterization of FD-iPSC derived neural crest precursor cells

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